Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study - The Lancet
Farmalisa - Spinraza is a medicine used to treat 5q spinal muscular atrophy (SMA), a genetic disease that causes weakness and wasting of the muscles including the lung muscles. The disease is
Roche's low-price Evrysdi will take 'meaningful' SMA share from Biogen's Spinraza: analyst | FiercePharma
Biogen's blockbuster rare disease drug could be in trouble
Spinraza 12 mg solution for injection - Summary of Product Characteristics (SmPC) - (emc)